Pompe Alliance heads to WORLD Symposium 2026 to highlight new Mental Health for Rare therapist training program to ...
PHILADELPHIA, PA — Aro Biotherapeutics reported interim data from a Phase 1b study of ABX1100, an investigational therapy for late-onset Pompe disease, showing the drug was generally well tolerated ...
Pompe disease is a rare metabolic disorder. It’s marked by a deficiency in lysosomal alpha-glucosidase. Your body needs this enzyme to break down stored glucose, which is called glycogen. When your ...
If you or your child has Pompe disease, it's important to know that each case is different, and that doctors have treatments to help manage it. Pompe disease happens when your body can't make a ...
Megan Crowley attends a joint session of the U.S. Congress. (Photo by Win McNamee/Getty Images) During his joint address to Congress tonight, Feb. 28, President Donald Trump called special attention ...