Jon Anning, a Slippery Rock University professor, has done extensive research on effects and treatment for Duchenne muscular ...

SOLVE FSHD, a venture philanthropy organization dedicated to accelerating treatments for facioscapulohumeral muscular ...

The EMA has backed broader pediatric use of Agamree and Crysvita, lowering age thresholds for rare genetic diseases affecting muscle and bone development.

Investigational deramiocel is back under FDA review again ...

Santhera Pharmaceuticals (SIX: SANN) today announced that the Committee for Medicinal Products for Human Use (CHMP) of the European Medicines Agency (EMA) has adopted a positive opinion recommending ...

Learn how to exercise safely with Duchenne muscular dystrophy, for your flexibility, mobility, and overall health, without ...

Your muscles need continuous maintenance to stay strong and healthy. Duchenne muscular dystrophy (DMD) happens when there is a change in a person's genetic instructions that affects the production of ...

Duchenne muscular dystrophy (DMD) is a genetic condition caused by a change, or mutation, in the DMD gene. This gene normally tells the body how to make dystrophin, a protein that helps protect ...

Burn Boot Camp 'Be Their Muscle' Campaign to benefit Muscular Dystrophy Association throughout April 2026 Burn Boot Camp celebrates 10 years of partnership with the Muscular Dystrophy Association, ...

Emma Ciafaloni, MD, FAAN, dives into the latest developments in gene therapy for muscular dystrophies, focusing on Duchenne muscular dystrophy, and discusses challenges, genetic causes, and the ...

We hypothesize that Duchenne muscular dystrophy and autism spectrum disorder/pervasive developmental disorder co-occur with a greater than random frequency. In this study, we set out to reject the ...

Santa Cruz community raises $97,000 for adaptive van for boy with Duchenne Muscular Dystrophy ...